New tools and delivery vehicles for CRISPR are only truly beneficial if we can simultaneously improve the affordability and access.

Sanjana discusses the large question his lab is trying to answer: "How can we efficiently identify which regions or genome drive disease?" ...

Large-scale study defines genetic architecture of stuttering; findings point to 48 genes associated and highlight neurological risk pathways.

Sarepta Therapeutics said it will resume shipments of its gene therapy Elevidys® (delandistrogene moxeparvovec-rokl) “imminently” to ambulant patients with Duchenne muscular dystrophy (DMD), ending a ...

The AI model, GeneAgent, reduces hallucinations for gene-set analysis by autonomously interacting with biology databases to verify output.

A new physiological salt-based method enables high-resolution transcription factor mapping in small and single-cell samples.

Improved understanding of how bacterial defense mechanisms operate may help scientists select phages with the best chance of ...

The UAE Pangenome Reference is freely available to support research into genetic disorders, disease predisposition, and population health.

Ivermectin is an effective strategy to control malaria transmission, according to a trial in Kenya, which showed a 26% reduction in new infections.

The molecular rules underlying autophagy of mitochondria, or mitophagy, provide therapeutic applications for neurodegeerative disease.

Abivax dazzled investors and analysts with positive data from a pair of Phase III induction trials assessing obefazimod in adults with moderately to severely active ulcerative colitis. The results ...

The FDA is investigating the death last month of an eight-year-old boy in Brazil who had received Sarepta Therapeutics’ Elevidys® (delandistrogene moxeparvovec-rokl)—though the company and its ...