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Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.
In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy in Philadelphia.
PHILADELPHIA — A baby ... gene editing treatment made just for him. Researchers described the case in a new study, saying he’s among the first to be successfully treated with a custom therapy ...
A personalized gene editing therapy was successfully used to treat an infant with CPS1 deficiency ... that involved a personalized gene-editing therapy developed and administered in less than a year. ...
“The first time you're putting a new drug into a baby is scary,” says Ahrens-Nicklas to NPR. “No one has done this before. No one has developed a personalized gene-editing therapy for an infan ...
The process, from diagnosis to treatment, took only six months and marks the first time the technology has been successfully deployed ... Medicine at the University of Pennsylvania (Penn) developed ...
In a medical first, a 9½-month-old baby named KJ has become the first person to receive a custom-made ... in a personalised CRISPR-based gene-editing therapy created in record time, and it ...
A baby born with a rare genetic disease is "growing and thriving" after getting bespoke gene therapy. It's the first time anyone ... from Clifton Heights, Pennsylvania, has a rare metabolic ...
A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers ...