A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new ...

LOS ANGELES, May 15 (Xinhua) -- In a groundbreaking medical milestone, U.S. researchers have successfully developed and delivered a personalized gene-editing therapy to treat an infant suffering ...

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to successfully receive a personalized CRISPR gene editing therapy. The ...

A research team has developed and safely delivered a personalized gene editing therapy to treat ... six months and marks the first time the technology has been successfully deployed to treat ...

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke therapies can be widely applied ...

K. J.—now 9 and a half months old—has received three doses of the therapy and has shown no adverse effects. He’s the first person known to receive a tailor-made gene-editing treatment.

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

A baby boy with a devastating genetic disease is thriving after becoming the first known person to receive ... these gene and cell therapies,” says Arkasubhra Ghosh, who studies gene therapy ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ... among the first to be successfully treated with a custom therapy ...