Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new ...

After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...

A research team has developed and safely delivered a personalized gene editing therapy to treat ... six months and marks the first time the technology has been successfully deployed to treat ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke therapies can be widely applied ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ... among the first to be successfully treated with a custom therapy ...

PHILADELPHIA — A baby ... gene editing treatment made just for him. Researchers described the case in a new study, saying he’s among the first to be successfully treated with a custom therapy ...

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to successfully receive a personalized CRISPR gene editing therapy. The ...

The process, from diagnosis to treatment, took only six months and marks the first time the technology has been successfully ... Pennsylvania (Penn) developed the customized therapy using the gene ...