A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy in Philadelphia.

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to successfully receive a personalized CRISPR gene editing therapy. The ...

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

A research team has developed and safely delivered a personalized gene editing therapy to treat ... six months and marks the first time the technology has been successfully deployed to treat ...

Credit: Melimama / CC BY 2.0 An American baby, KJ Muldoon, born with a rare and life-threatening genetic disease, is growing normally after undergoing the first successful personalized gene therapy.

A baby who is the first patient in the world to be successfully treated with customized CRISPR gene editing therapy is ... at the University of Pennsylvania developed a personalized gene-editing ...

The process, from diagnosis to treatment, took only six months and marks the first time the technology has been successfully ... Pennsylvania (Penn) developed the customized therapy using the gene ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.