Currently, GenAns Biotech is conducting investigator-initiated trials for several gene therapies, including GA001 for ...

US Food and Drug Administration Commissioner Marty Makary said he’s trying to persuade Vinay Prasad, the agency’s former head ...

Sarepta Therapeutics (SRPT) stock in focus as report says company hired a Trump-linked lobbying firm after deaths linked to ...

CGT Global, a leading biotechnology company driving the development and delivery of innovative cell and gene therapies, today ...

A 26-year-old Downriver man seen at Children’s Hospital of Michigan in Detroit since infancy for a rare bleeding disorder in ...

The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients ...

The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...

Shares of drugmaker Sarepta Therapeutics surged in afterhours trading Monday after the company said it would resume shipping ...

If successful, the access model for sickle cell disease gene therapies could serve as a blueprint for other such treatments ...

Africa’s pioneering cell and gene therapy startup wants to transform transplant medicine and improve treatment options for ...

Gene therapy appears to be a promising approach for a subset of genetic deafness, although challenges remain with development ...